pediatric

The future of gene therapy for a rare pediatric autoimmune disease

by
Photo of Rosa Bacchetta, associate professor of pediatrics at Stanford University

Rosa Wand uses modern technologies, such as CRISPR, to develop new gene therapies for IPEX syndrome. Rose Wand Rosa Wand is an associate professor of pediatrics at Stanford University. His goal as a doctor-scientist is to use modern technologies in the laboratory to find cures for incurable pediatric diseases. Wand’s main focus was on the … Read more

New genetic sequencing technology is helping researchers find answers in rare pediatric disease cases

by
Translational Genomics Research Institute

The study identified the probable cause of the genetic disease in six families PHOENIX AND SAN DIEGO, July 10, 2023 /PRNewswire/ — New genetic sequencing technology from Element Biosciences has helped researchers at the Translational Genomics Research Institute (TGen), part of the City of Hope, identify likely genetic causes of the disorders in six of … Read more